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Evaluation of Iptacopan in Atypical Hemolytic Uremic Syndrome (aHUS): Design and Rationale of the Phase 3 Open-label Multicenter APPELHUS Study
Nidhi Sharma*, David Kavanagh, Larry A. Greenbaum, Arvind Bagga, Chien-Wei-Chen, Rajeshri G. Karki, Sajita Vasudevan, Alan Charney, Marion Dahlke and Fadi Fakhouri